Nucleic Acid Therapeutics: From Bench to Bedside Symposium
17-18 February 2027, Bilbao (Spain)
This two-day scientific course is designed to bridge the gap between preclinical research on nucleic acid therapeutics and their clinical application. Through lectures delivered by renowned experts, the program will provide a comprehensive overview of the translational pathway, including key scientific, regulatory, and strategic considerations. Emphasis will be placed on real-world insights, featuring both successful and unsuccessful case studies to highlight critical decision points and common pitfalls in development.
The course is structured into four thematic training blocks. “The Drug” will cover the essential data required prior to IND submission (including CMC, toxicology, and efficacy), the role of CROs, dose selection strategies, PK/PD considerations, delivery challenges, and the integration of AI in drug development. “The Patients” will explore natural history studies, patient-reported outcome measures (PROMs), and the selection of clinically meaningful and regulator-acceptable biomarkers and outcome measures, alongside the importance of incorporating the patient voice. “The Trials” will focus on clinical trial design, including regulatory pathways for rare diseases and oligonucleotide-based therapies. Finally, “The Stories” will present real-world examples from bench to bedside, including both successes and failures, as well as innovative approaches such as n-of-1 trials, offering a holistic and practical perspective on translational research.
PRICE
100 Euro, max 100 participants
LOCATION
The meeting will take place in Bilbao, Spain (17th and 18th of February 2027). Bilbao is easily accessible by plane, and the city centre is a 15-minute bus ride from its international airport. The city offers plenty of hotels, restaurants, and other amenities.
VENUE
The symposium will be held at BBK Kuna, a social innovation hub located in the heart of Bilbao. The venue brings together spaces designed for learning, collaboration and public engagement, making it a fitting setting for a meeting focused on translating scientific innovation into patient impact. Scientific sessions will take place in Sala Ganbara, a bright, stage-equipped space designed for talks and presentations, with capacity for up to 141 participants.
